Replacement Therapy for Inherited Enzyme Deficiency — Macrophage-Targeted Glucocerebrosidase for Gaucher's Disease
Barton, Norman W.; Brady, Roscoe O.; Dambrosia, James M.; Di Bisceglie, Adrian M.; Doppelt, Samuel H.; Hill, Suvimol C.; Mankin, Henry J.; Murray, Gary J.; Parker, Robert I.; Argoff, Charles E.
- 作者Barton, Norman W.; Brady, Roscoe O.; Dambrosia, James M.; Di Bisceglie, Adrian M.; Doppelt, Samuel H.; Hill, Suvimol C.; Mankin, Henry J.; Murray, Gary J.; Parker, Robert I.; Argoff, Charles E.
- 卷第324卷
- 期第21期
- 印刷ISSN0096-6762
- 电子ISSN1533-4406
- 文件大小2462.07KB
- 发表时间1991
- DOI10.1056/nejm199105233242104
- 页码1464-1470