T.O.4 Safety and efficacy results from a randomized, double-blind, placebo-controlled study of alglucosidase alfa for the treatment of Pompe disease in juveniles and adults
P. Laforet; P.R. Clemens; D. Corzo; D. Escolar; J. Florence; A. van der Ploeg; S. Lake; J. Mayhew; A. Pestronk; B. Rosenbloom; A. Skrinar; M. Wasserstein
- 作者P. Laforet; P.R. Clemens; D. Corzo; D. Escolar; J. Florence; A. van der Ploeg; S. Lake; J. Mayhew; A. Pestronk; B. Rosenbloom; A. Skrinar; M. Wasserstein
- 卷第18卷
- 印刷ISSN0960-8966
- 文件大小55.94KB
- 发表时间2008
- DOI10.1016/j.nmd.2008.06.379