Myeloid driven stem cell gene therapy corrects a mouse model of Mucopolysaccharidiosis IIIA
Sergijenko, Ana; Langford-Smith, Alexander; Liao, Ai Yin; Pickford, Claire; McDermott, John; Langford-Smith, Kia; Merry, Catherine; Jones, Simon; Wraith, Ed; Wynn, Robert; Wilkinson, Fiona; Bigger, Brian
- 期刊名称Molecular Genetics and Metabolism
- 作者Sergijenko, Ana; Langford-Smith, Alexander; Liao, Ai Yin; Pickford, Claire; McDermott, John; Langford-Smith, Kia; Merry, Catherine; Jones, Simon; Wraith, Ed; Wynn, Robert; Wilkinson, Fiona; Bigger, Brian
- 卷第108卷
- 期第2期
- 印刷ISSN1096-7192
- 文件大小66.56KB
- 发表时间2013-2
- DOI10.1016/j.ymgme.2012.11.223