AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models
Vasireddy, Vidyullatha; Mills, Jason A.; Gaddameedi, Rajashekhar; Basner-Tschakarjan, Etiena; Kohnke, Monika; Black, Aaron D.; Alexandrov, Krill; Zhou, Shangzhen; Maguire, Albert M.; Chung, Daniel C.; Mac, Helen; Sullivan, Lisa; Gadue, Paul; Bennicelli, Jeannette L.; French, Deborah L.; Bennett, Jean; Lewin, Alfred
- 期刊名称PLoS ONE
- 作者Vasireddy, Vidyullatha; Mills, Jason A.; Gaddameedi, Rajashekhar; Basner-Tschakarjan, Etiena; Kohnke, Monika; Black, Aaron D.; Alexandrov, Krill; Zhou, Shangzhen; Maguire, Albert M.; Chung, Daniel C.; Mac, Helen; Sullivan, Lisa; Gadue, Paul; Bennicelli, Jeannette L.; French, Deborah L.; Bennett, Jean; Lewin, Alfred
- 卷第8卷
- 期第5期
- 电子ISSN1932-6203
- 文件大小1883.07KB
- 发表时间2013-5-7
- DOI10.1371/journal.pone.0061396