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AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

Vasireddy, Vidyullatha; Mills, Jason A.; Gaddameedi, Rajashekhar; Basner-Tschakarjan, Etiena; Kohnke, Monika; Black, Aaron D.; Alexandrov, Krill; Zhou, Shangzhen; Maguire, Albert M.; Chung, Daniel C.; Mac, Helen; Sullivan, Lisa; Gadue, Paul; Bennicelli, Jeannette L.; French, Deborah L.; Bennett, Jean; Lewin, Alfred
  • 期刊名称PLoS ONE
  • 作者Vasireddy, Vidyullatha; Mills, Jason A.; Gaddameedi, Rajashekhar; Basner-Tschakarjan, Etiena; Kohnke, Monika; Black, Aaron D.; Alexandrov, Krill; Zhou, Shangzhen; Maguire, Albert M.; Chung, Daniel C.; Mac, Helen; Sullivan, Lisa; Gadue, Paul; Bennicelli, Jeannette L.; French, Deborah L.; Bennett, Jean; Lewin, Alfred
  • 卷第8卷
  • 期第5期
  • 电子ISSN1932-6203
  • 文件大小1883.07KB
  • 发表时间2013-5-7
  • DOI10.1371/journal.pone.0061396
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