Glycosylation independent lysosomal targeting of alpha-n-acetylglucosaminidase confers highly efficient enzyme uptake into critical cellular targets of disease pathogenesis in mucopolysaccharidosis type IIIB

• 期刊名称Molecular Genetics and Metabolism
• 作者Yogalingam, Gouri; Prill, Heather; Lee, Amanda; Christianson, Terri; Tiger, Pascale M.N.; Yip, Bryan K.; Lo, Melanie J.; Holtzinger, John; Berguig, Geoffrey; Aoyagi-Scharber, Mika; Fitzpatrick, Paul; Lawrence, Roger; Crawford, Brett; LeBowitz, Jonathan H.
• 卷第117卷
• 期第2期
• 印刷ISSN1096-7192
• 文件大小51.16KB
• 发表时间2016-02
• DOI10.1016/j.ymgme.2015.12.491