360. Genotype/Phenotype Correlation of Cellular Function and AAV-Mediated Gene Delivery to Treat Xeroderma Pigmentosum - Cockayne Syndrome (XP - CS)
Rizzo, Skylar; Donate, Amy L.; Jones, Michael; Manko, Kelsey; Santostefano, Katherine E.; Terada, Nao; Alkuraya, Fowzan S.; Kang, Peter B.; Pacak, Christina A.
- 期刊名称Molecular Therapy
- 作者Rizzo, Skylar; Donate, Amy L.; Jones, Michael; Manko, Kelsey; Santostefano, Katherine E.; Terada, Nao; Alkuraya, Fowzan S.; Kang, Peter B.; Pacak, Christina A.
- 卷第24卷
- 印刷ISSN1525-0016
- 文件大小336.82KB
- 发表时间2016-05
- DOI10.1016/s1525-0016(16)33169-0