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5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency

5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency

Mueller, Christian; Gernoux, Gwladys; Gruntman, Alisha M.; Borel, Florie; Reeves, Emer P.; Calcedo, Roberto; Rouhani, Farshid N.; Yachnis, Anthony; Humphries, Margaret; Campbell-Thompson, Martha; Messina, Louis; Chulay, Jeffrey D.; Trapnell, Bruce; Wilson, James M.; McElvaney, Noel G.; Flotte, Terence R.
  • 期刊名称Molecular Therapy
  • 作者Mueller, Christian; Gernoux, Gwladys; Gruntman, Alisha M.; Borel, Florie; Reeves, Emer P.; Calcedo, Roberto; Rouhani, Farshid N.; Yachnis, Anthony; Humphries, Margaret; Campbell-Thompson, Martha; Messina, Louis; Chulay, Jeffrey D.; Trapnell, Bruce; Wilson, James M.; McElvaney, Noel G.; Flotte, Terence R.
  • 印刷ISSN1525-0016
  • 文件大小2004.25KB
  • 发表时间2017-4
  • DOI10.1016/j.ymthe.2017.03.029
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