5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency
Mueller, Christian; Gernoux, Gwladys; Gruntman, Alisha M.; Borel, Florie; Reeves, Emer P.; Calcedo, Roberto; Rouhani, Farshid N.; Yachnis, Anthony; Humphries, Margaret; Campbell-Thompson, Martha; Messina, Louis; Chulay, Jeffrey D.; Trapnell, Bruce; Wilson, James M.; McElvaney, Noel G.; Flotte, Terence R.
- 期刊名称Molecular Therapy
- 作者Mueller, Christian; Gernoux, Gwladys; Gruntman, Alisha M.; Borel, Florie; Reeves, Emer P.; Calcedo, Roberto; Rouhani, Farshid N.; Yachnis, Anthony; Humphries, Margaret; Campbell-Thompson, Martha; Messina, Louis; Chulay, Jeffrey D.; Trapnell, Bruce; Wilson, James M.; McElvaney, Noel G.; Flotte, Terence R.
- 印刷ISSN1525-0016
- 文件大小2004.25KB
- 发表时间2017-4
- DOI10.1016/j.ymthe.2017.03.029