Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study
Walter, Maggie C.; Wenninger, Stephan; Thiele, Simone; Stauber, Julia; Hiebeler, Miriam; Greckl, Eva; Stahl, Kristina; Pechmann, Astrid; Lochmüller, Hanns; Kirschner, Janbernd; Schoser, Benedikt
- 期刊名称Journal of Neuromuscular Diseases
- 作者Walter, Maggie C.; Wenninger, Stephan; Thiele, Simone; Stauber, Julia; Hiebeler, Miriam; Greckl, Eva; Stahl, Kristina; Pechmann, Astrid; Lochmüller, Hanns; Kirschner, Janbernd; Schoser, Benedikt
- 印刷ISSN2214-3599
- 电子ISSN2214-3602
- 文件大小315.22KB
- 发表时间2019-09-28
- DOI10.3233/JND-190416
- 页码1-13