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Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study

Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study

Walter, Maggie C.; Wenninger, Stephan; Thiele, Simone; Stauber, Julia; Hiebeler, Miriam; Greckl, Eva; Stahl, Kristina; Pechmann, Astrid; Lochmüller, Hanns; Kirschner, Janbernd; Schoser, Benedikt
  • 期刊名称Journal of Neuromuscular Diseases
  • 作者Walter, Maggie C.; Wenninger, Stephan; Thiele, Simone; Stauber, Julia; Hiebeler, Miriam; Greckl, Eva; Stahl, Kristina; Pechmann, Astrid; Lochmüller, Hanns; Kirschner, Janbernd; Schoser, Benedikt
  • 印刷ISSN2214-3599
  • 电子ISSN2214-3602
  • 文件大小315.22KB
  • 发表时间2019-09-28
  • DOI10.3233/JND-190416
  • 页码1-13
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