![5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency]()
5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin DeficiencyMueller, Christian; Gernoux, Gwladys; Gruntman, Alisha M.; Borel, Florie; Reeves, Emer P.; Calcedo, Roberto; Rouhani, Farshid N.; Yachnis, Anthony; Humphries, Margaret; Campbell-Thompson, Martha; Messina, Louis; Chulay, Jeffrey D.; Trapnell, Bruce; Wilson, James M.; McElvaney, Noel G.; Flotte, Terence R. · Molecular Therapy · 2017