![Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study]()
Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational StudyWalter, Maggie C.; Wenninger, Stephan; Thiele, Simone; Stauber, Julia; Hiebeler, Miriam; Greckl, Eva; Stahl, Kristina; Pechmann, Astrid; Lochmüller, Hanns; Kirschner, Janbernd; Schoser, Benedikt · Journal of Neuromuscular Diseases · 2019